Rare Disease Day 2025: 10 recent FDA approvals for rare diseases
In honor of Rare Disease Day, here are 10 new treatments approved by the FDA to treat rare diseases over the past year.
All articles by Rosemary
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Study: Off-label treatment shows promise in PBC
Cholesterol-lowering medications known as fibrates, often used off-label to treat PBC. showed promising results in a recent study.
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PBC Ambassador
PBC Ambassador
